Niemann-Pick Disease Type C Archives - The Children's Inn at NIH

Timeline – 2010-2017 - The Children's Inn at NIH

Experimental treatment for Niemann-Pick disease type C1 appears safe, effective NICHD - Eunice Kennedy Shriver National Institute of Child Health and Human Development

Timeline – 2010-2017 - The Children's Inn at NIH

A new regulatory mechanism of STARD1 in Niemann-Pick disease type C (NPC), discovered

2011 - NIH Clinical Center - National Institutes of Health

Progress on Niemann-Pick disease type C1 at the NIH Clinical Center

Timeline – 2010-2017 - The Children's Inn at NIH

A hopeful therapy for Niemann-Pick C diseases - The Lancet

Niemann-Pick disease type C clinical database: cognitive and coordination deficits are early disease indicators, Orphanet Journal of Rare Diseases

Download - United Way of Central Maryland

Niemann-Pick disease type C clinical database: cognitive and coordination deficits are early disease indicators, Orphanet Journal of Rare Diseases