TRIALS: A Fight for Children with Niemann-Pick Type C, a Fatal Genetic Disease
Por um escritor misterioso
Last updated 12 abril 2025

Children with Niemann-Pick Type C (NPC), their parents and scientists seeking a treatment for this fatal genetic disease. WSJ follows this 6-year fight.

Topic · Rare disease ·

delta – Columbus Children's Foundation

TRIALS: A Fight for Children with Niemann-Pick Type C, a Fatal Genetic Disease
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