Niemann Pick Disease - an overview
Por um escritor misterioso
Last updated 20 fevereiro 2025
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Miglustat in Niemann-Pick disease type C patients: a review, Orphanet Journal of Rare Diseases
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Niemann Pick Disease - Rivin
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Sphingomyelinase Deficiency: Practice Essentials, Pathophysiology, Etiology
Niemann–Pick disease
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Niemann-Pick Disease - Pediatrics - Medbullets Step 2/3
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IJMS, Free Full-Text
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What is Niemann Pick Type C - Race for Adam
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Natural history and management of liver dysfunction in lysosomal storage disorders
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Niemann-Pick disease: Causes, symptoms, treatment, and more
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