Treating Niemann-Pick Disease Type C

Compartilhe seus vídeos com amigos, familiares e todo o mundo

Niemann-Pick disease type C in Adults.pptx

Niemann–Pick Disease Type C

IJMS, Free Full-Text

Niemann-Pick Disease Type C - cyclotherapeutics

Advancements in Niemann-Pick Disease Type C Treatments

About NPD - International Niemann-Pick Disease Alliance (INPDA)

Elevation of plasma lysosphingomyelin-509 and urinary bile acid metabolite in Niemann-Pick disease type C-affected individuals - Top Articles selected by the Editor - Molecular Genetics and Metabolism Reports - Journal - Elsevier

Parents of twins with Niemann-Pick find a treatment

Two-Year-Old Kamryn Living with Niemann-Pick Disease Type C (NPC) - The Children's Inn at NIH

Acid Sphingomyelinase Deficiency - Symptoms, Causes, Treatment

Full article: New therapies in the management of Niemann-Pick type C disease: clinical utility of miglustat

Drug reformulation may improve treatment of Niemann-Pick type C disease [PreClinical]

Molecular mechanism(s) of neurodegeneration in Niemann-Pick type C disease - Ruđer Bošković Institute

Critical role for glycosphingolipids in Niemann-Pick disease type C: Current Biology

IJMS, Free Full-Text